SAREPTA THERAPEUTICS INC

About

Sarepta Therapeutics is a biotechnology company focused on the discovery and development of precision genetic medicines to treat rare neuromuscular diseases. The company has established a leading position in the treatment of Duchenne muscular dystrophy (DMD) through its portfolio of exon-skipping therapies and gene transfer technologies. Sarepta leverages multiple platforms, including RNA and gene therapy, to advance its pipeline of potential treatments for rare, life-limiting conditions.